In plain language. Written by scientists. uniQure reports that after 4 years, people given high-dose AMT-130 continue to show signs of slower HD progression, providing hope for their recent regulatory ...
September brought progress across the HD research landscape. From brain waves and visual thinking to DNA repeats, nutrition, ...
Day 1 of HD2026 is a wrap! From what human brains can teach us about HD, to HTT1a, somatic CAG expansion and the normal biology of HTT, today’s talks spanned the spectrum from fundamental biology to ...
One of the biggest challenges in clinical research is making the most of the information that trials generate. A solution to this is to share data between stakeholders so that everyone can learn from ...
⏱️6 min read | PROTACs act like a precision pruning tool, trimming away toxic huntingtin protein while leaving the healthy form intact. In cells and HD mice, this targeted clean-up improved health and ...
New 12-month data from Skyhawk’s SKY-0515 is in and all four measures that make up the cUHDRS are at or above baseline, beating expected natural decline. Plus, a first look at expanding US trial sites ...
Scientists have intensely studied the genetics of Huntington’s disease (HD) since the gene responsible was discovered in 1993. Unlike many other genetic diseases, where a change in one or a few DNA ...
On December 3, 2024 a study site gave word that the very first person received a new drug, called ALN-HTT02, as part of a ...
Four years after a single treatment, the high-dose AMT-130 group continues to show encouraging signs of slower HD progression ...
A review of 23 studies found that EEG changes were linked to disease progression and clinical measures in HD. While more research is needed, EEG holds potential to become a simple, non-invasive ...
You may have heard the saying, “you can’t run on empty.” A person living with HD may be eating regular meals, or even seem ...
Vico Therapeutics’ Huntington’s disease drug VO659 is now being tested just twice a year, and the FDA has cleared the way for US trials to begin later this year. Like other ASOsASOs A type of gene ...
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