ainvest

Design Therapeutics: The 12-Week DT-216P2 Readout, Not the May Data, Is the Real Test - 'Hold'

When Design Therapeutics DSGN+0.82%, Inc. (DSGN) reported four-week results for DT-216P2 in May, biotech 865238-0.87% ...
BIOENGINEER

Gabrielle Lévy: The Forgotten Neurologist Who Described a Hereditary Syndrome

In the crowded history of early twentieth-century neurology, the names that survive in eponyms are usually those of men. Yet one of the most elegant clinical descriptions of a hereditary neurological ...
The Leamington Observer

Young Stratford mum campaigns for drug that will prolong her life

Charlotte Casey, aged 25, and her 28 year-old sister Olivia Dews suffer from a rare genetic condition called Friedreich’s ...
Rare Disease Advisor

Study Sheds Light on the Mechanisms Underlying Myocardial Injury in ATTR-CM

Higher levels of high-sensitivity cardiac troponin T were independently associated with lower myocardial capillary density in ...

Larimar Therapeutics Strengthens Executive Leadership with Appointment of John Harlow as President and Chief Operating Officer

Inc. (Larimar) (Nasdaq: LRMR), a clinical-stage biotechnology company focused on developing treatments for complex rare diseases, today announced the appointment of John Harlow as President and Chief ...