Amanda Barnes, 49, held a solo wedding celebration after being diagnosed with incurable breast cancer and deciding she did not want to die without fulfilling her dream of becoming a bride. The ...

The first global assessment of rare neurological diseases in children finds rising prevalence and disability from 1990 to 2021, declining mortality, and a projected 11.83 percent increase in cases by ...

When the aging brain misfires, the results can be astonishing and a little alarming.

A seven-year Dutch study shows that a single baseline blood measurement of neurofilament light chain predicts the pace of ...

Conscience, a Canadian non-profit dedicated to enabling drug discovery through open science and collaboration for the advancement of accessible treatments, is proud to highlight two recently approved ...

Accepted for Priority Review with a PDUFA target action date of February 4, 2027; being granted Priority Review by the FDA underscores the significant unmet need for an oral targeted therapeutic optio ...

First Patient Dosed with JOTROL™ Marks Major Clinical Milestone for Jupiter Neurosciences’Phase 2a Study Evaluating Safety, Pharmacokinetics and ...

BeOne Medicines, a global oncology company, today announced the successful completion of negotiations with the pan-Canadian Pharmaceutical Alliance (pCPA) for TEVIMBRA® (tislelizumab for injection) in ...

Hello, I am Shizuya. I work as a company employee while living with a rare disease called CMT. Currently, I walk with a ...

Iqbal Sheikh, a resident of the Indian state of West Bengal, said that he has spent most of his time in water for the past five years.

IndoUSrare & GORD announce 2026 Abbey Meyers Khushi Bridging RARE Award honorees! Join us Nov. 1, Manassas, VA for an ...

SCY-770 was well tolerated with a favorable safety profile in healthy adult participants at higher doses than previously evaluated• Phase 2 ...