Today, the American Kidney Fund (AKF) and the IgA Nephropathy Foundation are on Capitol Hill with more than 80 advocates who are living with rare kidney diseases to urge elected officials to support ...

DANCING with the Stars judge Carrie Ann Inaba has spoken out about living with a rare medical condition. While the TV ...

Denny Ladkani lives with Duchenne Muscular Dystrophy, a rare genetic disease that causes progressive muscle degeneration and weakness throughout the body.

The number of treatments for rare genetic disorders is expected to increase sharply in the next several years.

First Patient Dosed with JOTROL™ Marks Major Clinical Milestone for Jupiter Neurosciences’Phase 2a Study Evaluating Safety, Pharmacokinetics and ...

Researchers from Kennedy Krieger Institute, University of Rochester Medicine and five other institutions released a new ...

When the aging brain misfires, the results can be astonishing and a little alarming.

Shionogi & Co., Ltd. (Head Office: Osaka, Japan; Chief Executive Officer: Isao Teshirogi, Ph.D.; hereafter "Shionogi") announced that its Board of Directors, at a meeting held on October 5, 2026, ...

IndoUSrare & GORD announce 2026 Abbey Meyers Khushi Bridging RARE Award honorees! Join us Nov. 1, Manassas, VA for an ...

The first global assessment of rare neurological diseases in children finds rising prevalence and disability from 1990 to 2021, declining mortality, and a projected 11.83 percent increase in cases by ...

Canada’s rare disease diagnostic challenge cannot be solved by genomics and data alone; it requires investment in the people, expertise, and clinical systems needed to recognize rare diseases earlier ...

The National Organization for Rare Disorders (NORD®) is honoring a distinguished group of biopharma industry leaders, medical ...